The most costly medication on the market as of late has just received FDA approval. Patients with the uncommon condition hemophilia B are given the medication, known as Hemogenic, which costs $3.5 million per dose.
What is gene therapy?
Gene therapy is a method for treating or curing disease by changing a person's DNA. Gene treatments can function in a variety of ways:
- swapping out a disease-causing gene for a healthy copy
- a disease-causing gene that is malfunctioning can be turned off
- the process of adding a new or altered gene to the organism in order to treat a condition
Products utilizing gene therapy are being investigated for the treatment of diseases like cancer, genetic disorders, and infectious diseases.
Most expensive gene therapy drug:
- Patients with the uncommon disease hemophilia B receive the Hemgenix medication, which costs $3.5 million per dosage.
- The less common kind of hemophilia, hemophilia B, is caused by a deficiency in a protein called protein IX.
- A person in every 40,000 has hemophilia B, and men make up the majority of its patients.
- Women are frequently carriers of the illness, showing no symptoms but passing it on to their offspring.
- Many patients require treatments once or more a week to stop significant bleeding from small cuts or bruises since they can be life-threatening.
- if the illness is not addressed, bleeding may develop that seeps into the brain and other organs, including the joints.
- Patients currently receive costly, repeated IVs of a protein that aids in blood clotting and stops bleeding.
- A single dose of the gene therapy medication Hemgenix is administered by IV infusion.
Hence, the drug costs $3.5 million per dose.
To learn more about gene therapy click on the link
brainly.com/question/315648
#SPJ4
